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Gene Therapy for β-Thalassemia

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Download this slideset for an expert-curated overview of gene therapy for β-thalassemia including the latest clinical data that may soon change practice.

Released: December 06, 2019

Expiration: December 04, 2020

No longer available for credit.

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Faculty

Janet L. Kwiatkowski

Janet L. Kwiatkowski, MD, MSCE

Professor of Pediatrics
Perelman School of Medicine of the University of Pennsylvania
Director, Thalassemia Program
Childrens Hospital of Philadelphia
Philadelphia, Pennsylvania

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Provided by Clinical Care Options, LLC

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Celgene

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Primary Author

Janet L. Kwiatkowski, MD, MSCE

Professor of Pediatrics
Perelman School of Medicine of the University of Pennsylvania
Director, Thalassemia Program
Childrens Hospital of Philadelphia
Philadelphia, Pennsylvania